Gene Therapy Diseases

New gene therapy slows progression of Huntington's disease

Breakthrough Gene Therapy Slows Huntington's Disease by 75%

"On the basis of these results, it seems likely AMT-130 will be the first licensed treatment to slow Huntington's disease, which is truly world-changing stuff," says Wild, who works at UCL's Huntingt...

Nature · 13h

Huntington’s disease treated for first time using gene therapy

Smithsonian Magazine · 10h

Experimental Gene Therapy Successfully Treats Huntington’s Disease for the First Time

· 1d

Huntington’s treatment slows disease for first time giving hope to families

Scientists have slowed the progression of Huntington’s disease for the first time with a “groundbreaking” new treatment.

· 1d

U.K. gene therapy trial effectively treats Huntington’s disease

· 1d

uniQure Stock Doubles On Promising Data From Huntington's Disease Trial

16h

Focus: Parkinson's disease at forefront of Bayer bet on cell and gene therapies

It's a test of CEO Bill Anderson's development credentials as patent expiries on blockbuster drugs threaten the group's long-term growth projects.

16h

Gene Therapy Could End Lifelong Transfusions For Rare Blood Disorder

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions.