Gene therapy holds the promise of preventing and curing disease by manipulating gene expression within a patient's cells.

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...

Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic ...

Despite its strong influence, APOE is not the sole cause of Alzheimer’s or other dementias. Even among people with the ...

Psoriasis is a common inflammatory skin disease linked to several long-term health conditions, such as heart disease, ...

Gene therapy drugs have the potential to cure some diseases, but some have a price tag of over a million dollars. Who gets access to them and who doesn't?

University of California San Diego-led team has discovered that restoring a key cardiac protein called connexin‑43 in a mouse ...

AskBio Inc., an RTP-based gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, has received U.S. Food and Drug Administration (FDA) acceptance of its ...

SynGenSys, a biotechnology company designing synthetic gene promoter systems to address critical bottlenecks in biopharma manufacturing and enhance cell and gene therapy development, today announced ...