Researchers developed a single LRS assay that can detect and characterize genetic variations causing inherited myopathies, ...

Age, comorbidity, disease risk, and donor type should guide conditioning intensity in myelodysplastic syndromes (MDS), rather ...

The results of a retrospective study of patients with Gaucher disease (GD) type 1 may support earlier screening for Parkinson ...

Higher CD34+ cell and colony-forming unit-granulocyte/macrophage (CFU-GM) doses were associated with better DFS in high-risk ...

Interstitial lung abnormalities have an adverse effect on long-term survival after non–small cell lung cancer resection, ...

RBCs in patients with low-risk MDS carry distinct physiological abnormalities that go beyond ineffective erythropoiesis.

Switching from emicizumab to denecimig without a washout period in adolescents and adults with hemophilia A is well tolerated ...

The FDA has approved an update to the label of sotatercept-csrk to include data from a trial, which tested the drug in newly ...

CAR T-cell therapy produced a 68% overall response rate in 194 patients with PCNSL, but progression-free survival fell to 25% ...

The results of a new study show miR-196a may reduce mHTT through Rad23b, suggesting the protein as a potential target in HD.

HPS has 11 subtypes; 100% of patients with type 1, 2, or 4 will develop pulmonary fibrosis, usually by their mid-30s.

Findings from a retrospective study conducted in Japan and published recently in Immunological Medicine have shown that ...