Researchers at Cedars-Sinai are working on a potential stem cell treatment for three siblings in California with an ultra ...

Columnist Ari Anderson has learned to use his time wisely so that he can enjoy fun activities while also completing the work ...

Keynote speaker Mindy Henderson redefines "impossible" ahead of MDA Engage: Chicago, taking place Sept. 25-26 at the Westin ...

Columnist Kevin Schaefer celebrates the approval of Isembyld for SMA, and remembers the relentless enthusiasm of his friend ...

After going viral on social media, columnist Sherry Toh says her eyes were opened to how much people engage with content that ...

Children and adults with SMA and their caregivers may experience clinically relevant mental health symptoms, a German study found.

A European survey found that while treatment options have expanded, SMA patients still face limited access to medicines and ...

A new blood test detected 95% of homozygous SMN1 deletions, the cause of most SMA cases, with results available in about an ...

The muscle-strengthening agent apitegromab, now Isembyld, has been approved in the U.S. as an add-on treatment for spinal muscular atrophy.

Columnist Connie Chandler's relationship with her wheelchair is complicated, but she's learned it helps her tell her story ...

Columnist Brianna Albers used to trust her doctors completely, but having a rare disease forced her to recognize they don't know everything.