In a real-world study, nearly half of adults with LGS, DS, or TSC who added CBD experienced a 50% or greater reduction in ...
Bezuclastinib produced significantly greater symptom improvement than placebo at 24 weeks in adults with symptomatic ...
Growing evidence suggests viral infections can exacerbate myasthenia gravis (MG) or even contribute to its development.
Severe fatigue remains common among patients with PNH receiving long-term eculizumab and appears to stem from more than anemia alone.
Turkish patients with genetically confirmed PMDs are still likely to be managed with empirical vitamin and cofactor ...
A PCR assay may determine a fetus’s RhD status even in the presence of maternal RhD variants, helping to assess the risk of HDFN.
Two cases of SM with associated hematologic neoplasm demonstrated how clinical severity, molecular findings, and treatment ...
In a recent study, children with severe AAV showed reduced disease activity after plasma exchange and intensive ...
Gabapentin reduced cough and improved cough-related quality of life in patients with IPF, according to a recent study.
The FDA granted Orphan Drug Designation to a 21-amino-acid peptide targeting expanded CAG-repeat RNA for the treatment of HD.
The prevalence of obstructive sleep apnea is "remarkably high" among patients with IPF, according to a recent study.
GENESIS-IPF-3 is the first phase 3 trial of a therapy discovered and engineered with generative AI for IPF, per a recent ...
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