For the first time, Huntington's disease has been successfully treated. That's according to researchers in London. Doctors ...

An experimental gene therapy was found to slow the progression of Huntington's disease, marking a major step toward a ...

An experimental gene therapy has slowed the progression of Huntington’s disease by 75 percent, according to results reported by the biotechnology company uniQure this week.

A team led by scientists at Harvard Medical School, Massachusetts General Hospital, and the Broad Institute of MIT and ...

UniQure's experimental gene therapy for Huntington's disease slowed progression of the brain disorder by 75% in an early-to-mid stage study, it said on Wednesday.

HHS is taking new steps to speed the development and review of new cell and gene therapies in the U.S. Three things to know: 1. The FDA published three draft guidances Sept. 24 detailing strategies ...

The American Society of Health-System Pharmacists has launched the  ASHP Center for Next Generation Therapeutics, aimed at supporting hospitals and ...

Using an incredibly delicate form of brain surgery called stereotactic surgery, tiny tubes are inserted into the brain and ...

Scientists from the Gray Faculty of Medical & Health Sciences at Tel Aviv University introduced an innovative gene therapy ...

University of Iowa researchers developed a gene therapy that could prevent craniosynostosis, a condition where babies’ skull bones fuse too early, potentially eliminating the need for invasive skull ...

The therapy is expected to block abnormal blood vessel growth, limit vascular leakage, and reduce retina damage. The Food and Drug Administration (FDA) has granted Fast Track designation to SAR402663 ...

This article is part of Nature Outlook: Skin, an editorially independent supplement produced with financial support from LEO Pharma. About this content. KaDee Troop is the mother of seven adopted ...